Research Grant
[Cite as https://purl.org/au-research/grants/nhmrc/1050277]Researchers: A/Pr Matthias Klugmann (Principal investigator)
Brief description White matter diseases are debilitating childhood disorders caused by defects in the insulating myelin sheath normally covering and protecting the nerve fibres from damage. There is currently no effective treatment but the delivery of a genetic medicine to the diseased myelin forming cells in the brain could be curative. This project aims at establishing the safe, efficient and non-invasive delivery of therapeutic genes to myelin forming cells as a gene therapy for white matter disorders.
Funding Amount $AUD 594,393.27
Funding Scheme Project Grants
Notes Standard Project Grant
- nhmrc : 1050277
- PURL : https://purl.org/au-research/grants/nhmrc/1050277
