grant

Development of a safe and effective treatment for neuropathology in MPS IIIA. [ 2009 - 2011 ]

Also known as: Treating children affected by progressive brain disease

Funded by National Health and Medical Research Council
Managed by University of Adelaide
Provided by   National Health and Medical Research Council

Research Grant

[Cite as https://purl.org/au-research/grants/nhmrc/565074]

Researchers: Prof John Hopwood (Principal investigator) ,  Dr Allison Crawley ,  Dr Kim Hemsley

Brief description MPS IIIA is an inherited disorder that results in progressive brain disease in affected children. The disorder cannot be treated at present because it has not been possible to find an effective way to deliver treatment to the brain. This project seeks to evaluate a method to overcome this problem. Findings in this project can be applied to other, similar disorders that affect the brain.

Funding Amount $AUD 665,320.10

Funding Scheme NHMRC Project Grants

Notes Standard Project Grant

Click to explore relationships graph
Help

Related Publications

  • Associated with Determination of the role of injection site on the efficacy of intra-CSF enzyme replacement therapy in MPS IIIA mice
    handle : 2440/97747
  • Associated with Disease stage determines the efficacy of treatment of a paediatric neurodegenerative disease
    handle : 2440/87175

Related Organisations

Related People

Subjects
321011 | Sanfilippo syndrome | animal model | enzyme therapy | incurable, progressive, neurological disease | inherited metabolic disorders | lysosomal storage disorder | targeted therapy | treatment of central nervous system pathology | treatment of lysosomal storage disorders |
Identifiers
Viewed: [[ro.stat.viewed]]
Saved to MyRDA Save to MyRDA