Research Grant
[Cite as https://purl.org/au-research/grants/nhmrc/1036656]Researchers: Dr Jane Seto (Principal investigator)
Brief description Therapeutic replacement of small, normal sections of the dystrophin gene can prevent muscle wasting in young dystrophic mice with mutations in dystrophin. This project attempts to apply the same principle to treat another inherited muscle disorder, caused by mutations in the FKRP gene. This approach can also potentially be used to enhance muscle regeneration and treat age related muscle atrophy, or synergistically applied with other therapies that target specific genetic mutations.
Funding Amount $AUD 347,264.87
Funding Scheme Early Career Fellowships
Notes CJ Martin Biomedical ECF
- nhmrc : 1036656
- PURL : https://purl.org/au-research/grants/nhmrc/1036656
